Transcript Slides
Putting the “c” in cGMP: How to Remain Current
“What Attorneys Need to Know”
FDLI
July 10, 2013
Washington D.C.
Roy Sturgeon, Ph.D.
President
Lachman Consultant Services Inc.
[email protected]
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Topics
How to Get and Stay Current
What’s the Industry Perspective?
Aggressive GxP Enforcement Environment
Increased Data Integrity Focus
During PAIs and Other Inspections
Accountability and Prosecution
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Industry Priorities/Strategies
Uninterrupted Supply of High Quality Approved
Products on Time at a Reasonable cost
Quality Culture
Compliance with Rules and Regulations
Janet Woodcock, MD, USFDA Mission:
To have a maximally efficient, agile, flexible
pharmaceutical manufacturing sector that reliably
produces high quality drug products without extensive
regulatory oversight.
Lachman Consultant Services Inc.
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Global Market Swamped in Product Recalls,
Enforcement and Shortages
Regulatory Agencies assertive with companies about recalls.
Global Regulatory Agencies (Except FDA) have mandatory recall
authority.
Overall enforcement environment , focus on corporate and
individuals, poster child criminal and civil actions - resulting in
aggressive company decisions to recall
Many recalls based on GMP “lack of assurance” of quality versus
actual/probable defects.
More aggressive recall classifications (I, II, III) and associated
product removal strategies
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When Do Attorneys Get
Involved?
Usually Late – “When the Sheriff is at the Door”
After 483s, WLs, Recalls, Seizures, Data Integrity, Problem
Resolution
Ideal - In Strategy Development/Reviews at Senior
Executive/Board Levels, Compliance Planning
In Deploying Appropriate Controls
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Advising on Corporate & Individual Liability
and Responsibility for GMPs
FDA deputy chief counsel for litigation Eric Blumberg calls
for greater use of the Park Doctrine and jail terms in
healthcare fraud prosecutions, holding executives personally
responsible (strict liability) for regulatory infractions, even
without personal knowledge or intent to defraud.
Glaxo Settlement Adds New ‘Financial Recoupment
Program’ (8-17-12) - This “puts at risk of forfeiture and
recoupment an amount equivalent to up to three years of
annual performance pay (i.e., annual bonus, plus long term
incentives) for an executive who is discovered to have been
involved in any significant misconduct”.
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July 30, 2012
Court allows HHS to ban executives from industry
GSK ex-Officials targeted?
Appeals Court upheld a 12-year ban from government
programs for former CEO Michael Friedman, general counsel
Howard Udell and former CSO Paul D. Goldenheim in the
government's case that was settled in 2007 for $634.5 million
over marketing of OxyContin.
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FDA - Focus on Risk
GMP & Product Quality
Risk Factors
Contamination Prevention
Sterility Assurance
Microbiological Quality
Cross Contamination
Intentional (melamine; OSCS)
Data Integrity
GxP Data and Records
Submissions
Global Sources
GMP
Drug Safety
REMS
Pharmacovigilance
Bioresearch Monitoring
GCP (Sponsors; Monitors; IRBs;
Investigators)
GLP Studies
BA/BE Studies
Unapproved New Drugs
Internet
“Grandfathered” NEW Drugs
Improper Sales/Marketing
Quality
DTC
Safety
Control/Practice of Sales Team
Counterfeits
Web Sites
Gray Market and Stolen Drugs
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Enforcement Priorities
Contamination Prevention –
micro, chemical, intrinsic,
extrinsic, particulates
High Risk Compounded
Drugs
Internet Health Fraud
Unapproved Drugs
Data Integrity
Response to Contamination
Events
Adverse Event reporting
Investigations Program
Supply Chain
Complaints
OOS/Rejections
CAPA Programs
Quality Systems/Quality
Culture
OTC Drug Quality
Security
CMOs and Material Vendor
Qualification
Field Alert Reporting
Prevention or Prompt
Mitigation of Drug
Shortages
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Getting Ready for PAI
What You Need to Know
Knowledge of Laws,
Regulations, Guidances,
Policies
Training (GMPs, Ethics, etc.)
Good Documentation
Data/ Record Keeping
Knowledge of FDA Processes
Capacity
Organized to Execute?
Infrastructure
Standards, SOPs and
Metrics
Enabling Documentation
Right People in Right
Positions
Clear Roles, Responsibilities
Evidence (raw data and
records)
Follow Up
and Accountabilities
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Assessments for PAI
Readiness for Commercial Manufacturing
Investigations/Trends
Materials Handling
Contamination
Procedures
Process Feasibility
Conformance to Application
Data Integrity
.
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FDA Has Not Forgotten
the Generic Drugs Scandal
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What is a GMP Violation?
What deems a drug adulterated?
• Distinguish from the facts of a drug
• “Most prosecuted cases turn on proof of failure to follow GMP
practices – NOT the final quality of the drug”
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Major Reasons for Failing PAIs
Not ready for inspection or lacks operational capability for
responsibilities described in CMC
General GMP Status is Unacceptable (i.e., “OAI”)
GMP Deficiencies for Pivotal Clinical, Scale-Up, Stability
and/or BE Batches
Data inconsistencies
Insufficient batch record detail to drive and document execution
Justification for critical process parameters and critical
ingredient and product quality attributes
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Top 10 FDA Domestic Inspection Citations October
2010 - October 2012
Testing and release for distribution
Cleaning /sanitizing /maintenance
SOPs not followed/documented
Training - operations, GMPs, written…
Written procdures not…
Control proceudres to monitor and…
Investigations of discrepancies/failures
Scientifically sound laboratory controls
Absence of written procedures
Procedures not in writng/fully followed
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50 100 150 200 250 300 350 400
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Prosecution
DOJ makes GMP Regulations “Top Area of Focus” for
2013
95% of Park Doctrine Prosecutions have been in last 6
Years – Targets Board Members and Senior Executives
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What is a GMP Violation?
What deems a drug adulterated?
• Distinguish from the facts of a drug
• “Most prosecuted cases turn on proof of failure to follow GMP
practices – NOT the final quality of the drug”
Lachman Consultant Services Inc.
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Major FDC Act Violations Unchanged
Submitting false and/or misleading
information to the agency
Falsification of GXP records,
regardless of whether submitted to
agency
Distributing a drug product in
violation of investigational or
approved requirements
False/misleading use, promotion or
advertising
Drug safety monitoring and
reporting violations
Adulteration of drug substance
or finished drug product
Commercial or clinical use
Not meeting appropriate,
established specifications
Contamination
Manufactured in violation of
GMP requirements,
regardless of whether
analytical specs met
Unlawful distribution of
clinical materials or physician
samples
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Significant Post-Approval Findings
Post approval inspections often triggered when PAIs are waived and when
there are > average # of FARs and Recalls. Significant findings:
Lack of justification for critical process parameters, operating ranges
and control strategies.
Scale-up to commercial process not adequately validated prior to
distribution
Stability testing commitments not met; unreported stability test failures;
expiry dates unsupported
Unreported/unapproved changes to material/component suppliers,
contractors, specifications, facilities, equipment, process, test methods,
etc.
Discrepancies suggesting fraud or deception
Unfulfilled application commitments
Inadequate Pharmacovigilance programs
Lachman Consultant Services Inc.
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How to Fix Significant GMP Deficiencies
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Data Integrity Issues - How They Happen
Non-Deliberate
› Raw data misplaced – lack of clarity/training in procedures to
require retention of all data
› Data misfiled, can’t be located
› Errors in transcription
› Lack of adequate review of final records
› Rushing to meet deadlines causes errors to be overlooked
Deliberate
› Fear of discovery of failure or error by management or regulators –
desire to “avoid pain”
› Desire to achieve objectives resulting in covering up errors
› Rare if a systemic effort to falsify records by management
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Fraudulent Practices
Creating passing test results without performing the test
Substituting test results from one sample/batch to another
Backdating records/reports
Falsifying GxP documents – submitted or not
Reporting only acceptable results (running “practice injections”
and deleting any unacceptable results)
Reporting unrealistic results
Data that looks “too perfect” or same
Forging signatures, sharing passwords, software that allows for
deletion of results/data by all analysts/employees
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What to Do
For alleged or suspected wrong doing, obtain assistance from
qualified/experienced third party expert:
Consultant(s) with experience in fraud Investigations
Attorney/Law Firm - internal and/or external
Establish the scope and breadth of the problem
Bracket dates when alleged wrong doing occurred
Determine if product(s), applications effected
Develop internal investigation plan
Identify / isolate suspect documents
Locate raw data
Compare raw data to summaries
Tabulate data and sort by each variable
Identify / resolve inconsistencies
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What to Do
(cont’d)
Examine firm’s organization
Examine roles, responsibilities and accountabilities
Identify personnel alleged/suspected of involvement
Determine scope of involvement of each employee
Consider higher ups - managers, directors, etc.
Conduct Interviews (by third party and attorney (s))
Investigate all work of suspected personnel
Determine root cause of problem:
Poorly defined procedures, roles, responsibilities, training gaps,
incompetence, deliberate wrongful acts, financial gain/incentives, others
Involve legal counsel in all decisions
Consult FDA’s “Points to Consider for Internal Reviews and Corrective
Action Operating Plans”
Take personnel action where justified by facts
Lachman Consultant Services Inc.
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Ethics and GMP Training
Importance of preserving raw data and reporting all data
including failing data in addition to passing data
Creating accurate data summaries and verifying raw data to
support the summaries (electronic and paper records)
Business ethics – adopt the elements of the HHS OIG seven
point compliance program for pharmaceutical companies
Include whistleblower protection and a telephone/email
“hot line” for reporting alleged wrongdoings
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Fix the Problem
NEVER alter / destroy original data, documents
Enter correct data or prepare addendum
Justify / explain errors
Preserve as part of formal record
Determine root cause
Correct and prevent root cause of errors
Re-audit following corrections (by independent third party
and internal auditors)
Assess the specific and system matters
Document and resolve any additional findings
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Conclusions
Firms must have strong quality and ethics programs and maintain
management oversight procedures and clear personnel policies
that prevent data integrity matters, be able to detect them if they do
occur, and deal with them effectively
Data integrity - focus and concern during any FDA inspection
Not all data integrity matters are “fraud”, isolated instances of data
integrity matter where not deliberate are easily remediated
A pattern or practice of data integrity matters, or the commission of
deliberate wrongful acts, are extremely serious and must be dealt
with timely and adequately
FDA has administrative and legal remedies it can apply when
companies fail to have the above in place and adequately in use
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Advice to Attorneys
from Dr. Mom
“It’s easier to keep firms out of
trouble than to get them out of
trouble”
AND a lot less expensive
.
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Thank You!
Roy Sturgeon, PhD
President
Lachman Consultants
Westbury, NY 11590
516-222-6222
Email: [email protected]
Website: www.lachmanconsultants.com
Lachman Consultant Services Inc.
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2011 Enforcement
Seizures – 8
Injunctions – 18
Convictions – 375
Warning Letters - >1700 (1200 Tobacco, 159 – Drugs &
Devices for 6 months)
Recalls – Drugs – 1616
Import Refusals - >27,000
Fines - > $4.5 Billion
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Corrective Actions by Company
Will depend on facts from investigation
Actions should include:
Communicate effectively with FDA and other law
enforcement agencies
Take actions and/or remove all personnel
(employees, contractors and others) who were or
may have been involved in wrongful acts
A credible investigation using a competent third
parties (consultants/attorneys)
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